PharmD Info

A forum for Indian Pharmacy Professionals

Share any Pharmaceutical related news with appropriate reference. Latest Pharmaceutical News, Indian Pharma News,
Forum rules: General rules are applicable for this forum- Find Here
  • User avatar
#2470
It’s a revolution when “US FDA” approved yesterday the FIRST gene-therapy medicine indicated for a disease other than cancer.

It’s “LUXTURNA” of “SPARK Therapeutics”.

There is a kind of vision-loss for people due to the defective gene namely “RPE65”.

“RPE65” gene produces a protein in our eye-cell which contributes to vision.

Vision-loss due to this “RPE65” gene is a hereditary disease and around 2000 people are being diagnosed in the USA every year.

“LUXTURNA” contains good “RPE65” genes and by administration of this to the eye can replace defective “RPE65” genes and thus can give vision.

Here, “trained”- virus carries the good “RPE65” genes to eyes.



Reference: https://www.fda.gov/NewsEvents/Newsroom ... 589467.htm
Similar Topics
Topics Statistics Last post
0 Replies 
474 Views
by Admin
0 Replies 
363 Views
by smith4u
0 Replies 
293 Views
by Admin
0 Replies 
255 Views
by Admin
0 Replies 
881 Views
by Freelancer

In recent years, the PharmD program has gained sig[…]

In today's dynamic healthcare landscape, pharmacis[…]

Are you aspiring to pursue a Master of Pharmacy (M[…]

PharmD Info - Highlights